Day

October 5, 2023

5
Oct
2023

Fulfilling the Promise of Sickle Cell Gene Therapy

Two gene therapies for sickle cell disease, CRISPR/Vertex’s exa-cel and Bluebird Bio’s lovo-cel, are being reviewed by the FDA and are likely to win US approval for sale by the end of the year. While it will take more time to fully establish long-term safety and efficacy of these therapies, they offer a glimmer of hope for a cure. This...
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